Article PubMed
Plos One  (2014)

Allele-specific knockdown of ALS-associated mutant TDP-43 in neural stem cells derived from induced pluripotent stem cells

Nishimura AL; Shum C; Scotter EL; Abdelgany A; Sardone V; Wright J; Lee YB; Chen HJ; Bilican B; Carrasco M; Maniatis T; Chandran S3; Rogelj B; Gallo JM; Shaw CE.